MDA Awards 18 New Grants, Totaling More Than $1.6M
The Muscular Dystrophy Association (MDA) announces the awarding of 18 new MDA grants totaling over $1.6 million toward neuromuscular disease research.
Category: Muscular Dystrophy
Muscular Dystrophy
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Muscular Dystrophy
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Sarepta Therapeutics Announces Scholarship Recipients
Sarepta Therapeutics Inc announces 15 recipients of Route 79, The Duchenne Scholarship Program created to recognize exceptional individuals living with Duchenne muscular dystrophy as they pursue their post-secondary education.
Muscular Dystrophy
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CureDuchenne Launches Supplemental Newborn Screening Initiative
CureDuchenne has launched a supplemental newborn screening initiative for Duchenne muscular dystrophy, in partnership with Brigham and Women's Hospital.
Impact of Chronic Inflammation May Spur New Duchenne Therapies
A new study reveals how chronic inflammation promotes muscle fibrosis, which could inform the development of new therapies for Duchenne muscular dystrophy (DMD), a fatal muscle disease.
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It’s Time to Fill the Boot Again
The Muscular Dystrophy Association (MDA), in partnership with the International Association of Fire Fighters (IAFF), launches the 2021 “Fill the Boot” fundraising campaign.
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Enhanced DuchenneXchange Features Improved Infrastructure and Functionality
The Duchenne community launches DuchenneXchange V2.0, an enhanced version of its collaborative digital platform and mobile app.
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CureDuchenne Invests in Entrada Therapeutics to Accelerate Drug Development
CureDuchenne Ventures is now funding and collaborating in Entrada Therapeutics’ Duchenne program, as was announced recently as part of Entrada’s latest financing from a group of investors.
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SMA Foundation and PTC Therapeutics Expand Research Partnership
The Spinal Muscular Atrophy (SMA) Foundation and PTC Therapeutics Inc have entered into a new collaboration focused on regenerative medicine to further advance scientific research in SMA and other neuromuscular disorders with the goal of developing new treatments.
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MDA Announces Virtual Conference Schedule
The Muscular Dystrophy Association (MDA) announces the schedule for the 2021 MDA Virtual Clinical and Scientific Conference, which will be held March 15-18.
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Gene Therapy for Duchenne Receives PPMD Grant Boost
Parent Project Muscular Dystrophy (PPMD) has awarded the University of Florida (UF) Wellstone Muscular Dystrophy Cooperative Center a grant for $348,891 for its research project to help understand and improve gene therapy for Duchenne.
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Duchenne UK, Parent Project Muscular Dystrophy, Announce Research Grant Recipient
Parent Project Muscular Dystrophy (PPMD) and Duchenne UK announce Professor Kanneboyina Nagaraju at Binghamton, the State University of New York, as the recipient of their Joint Research Grant Call of 2020.
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FDA Approves Targeted Treatment for Duchenne Mutation
The US Food and Drug Administration granted approval for Amondys 45 (casimersen) injection for the treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amenable to exon 45 skipping.
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Spina Bifida Could Result from ‘Mosaic Mutation’
Genetic mutations which occur naturally during the earliest stages of an embryo’s development can cause the severe birth defect spina bifida, University College London scientists suggest, in Nature Communications.
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MDA Rolls Out Its 39th Annual Shamrocks Campaign
The Muscular Dystrophy Association (MDA) launches its St Patrick’s Day fundraising program, the 39th annual MDA Shamrocks campaign.
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Parent Project Muscular Dystrophy Receives $100K Award to Address Neurobehavioral Issues
Parent Project Muscular Dystrophy (PPMD) announces a $100,000 sponsorship from the Duchenne Research Fund as part of PPMD’s new Brain Initiative.
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Important Spina Bifida Care Update
A special issue of the Journal of Pediatric Rehabilitation Medicine (JPRM) provides 20 evidence- and consensus-based updates to key sections of the 2018 “Guidelines for the Care of People with Spina Bifida” issued by the Spina Bifida Association (SBA).
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Virtual Town Hall Feb 3 to Commemorate Signing of MD-CARE Act
The Advocacy in Action Virtual Town Hall on February 3, hosted by Parent Project Muscular Dystrophy (PPMD), kicks off a year of activities recognizing the foundational work of 2001 that culminated with then-President George W. Bush signing the MD-CARE Act into law.
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THREAD Brings Uptick in Duchenne Registry Survey Completions in 2020
Year one of Parent Project Muscular Dystrophy’s The Duchenne Registry Mobile App, supported by the THREAD platform, has achieved impressive results, according to a news release.
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