REGENXBIO Presents Data from Trial of RGX-202 for Duchenne
REGENXBIO Inc. announced additional interim safety data and initial efficacy data from the Phase I/II AFFINITY DUCHENNE trial of RGX-202 for the treatment of Duchenne Muscular Dystrophy.
Category: Muscular Dystrophy
Muscular Dystrophy
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Muscular Dystrophy
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Parent Project Muscular Dystrophy Adds Riley Children’s Health to CDCC Program
The clinic at Riley Children's Health is now part of Parent Project Muscular Dystrophy's Certified Duchenne Care Center (CDCC) Program.
Muscular Dystrophy
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Volunteers to Gather Online to Celebrate Walk & Roll Effort to End FSHD
The FSHD Society Walk & Roll to Cure FSHD Livestream Celebration takes place Saturday, September 17, 8:30-11:30am Central, on Facebook.
Parent Project Muscular Dystrophy Announces Pediatric Certified Duchenne Care Center, Billings Clinic
Parent Project Muscular Dystrophy expands their Certified Duchenne Care Center Program with the certification of the Billings Clinic.
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Oxford-Harrington Rare Disease Centre to Advance Novel Treatment for Duchenne Muscular Dystrophy
The Oxford-Harrington Rare Disease Centre announce its support of a novel treatment for Duchenne muscular dystrophy.
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Sarepta Therapeutics Intends to Submit an Accelerated BLA for Its Gene Therapy to Treat Duchenne Muscular Dystrophy
Sarepta Therapeutics Inc announces its intent to submit a BLA seeking accelerated approval for SRP-9001 to treat individuals with Duchenne.
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Bionic Clothing Maker CIONIC Collaborates with Yves Behar’s fuseproject
CIONIC announces a collaboration with acclaimed designer Yves Behar and his world-renowned multidisciplinary design firm, fuseproject.
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Parent Project Muscular Dystrophy Certifies Pittsburgh Clinic
Parent Project Muscular Dystrophy adds the clinic at UPMC Children’s Hospital of Pittsburgh to its Certified Duchenne Care Center Program.
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Fulcrum Phase 3 REACH FSHD Clinical Trial Using AMRA Medical’s MRI Measurements
Fulcrum Therapeutics is using AMRA Medical’s muscle fat infiltration (MFI) as a secondary endpoint in its phase 3 FSHD clinical trial: REACH.
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Parent Project Muscular Dystrophy (PPMD) Announces Pediatric Certified Duchenne Care Center at St Louis Children’s Hospital
Parent Project Muscular Dystrophy expands its Certified Duchenne Care Program with the certification of the first clinic in St. Louis.
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How Does Duchenne Muscular Dystrophy Cause Heart Rhythm Problems?
Mutations that cause Duchenne muscular dystrophy slow electrical activity in the heart, causing abnormal heart rhythms, a study notes.
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AMRA Medical Continues to Advance FSHD Research with Whole-Body Measurements
AMRA Medical publishes results of its Fulcrum-sponsored study highlighting the development and use of a MRI protocol for muscle analysis.
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Parent Project Muscular Dystrophy Nominates Duchenne for RUSP
Parent Project Muscular Dystrophy nominates Duchenne to be part of Recommended Uniform Screening Panel (RUSP) for newborns.
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LGMD Community Celebrates Adoption of ICD-10 Diagnostic Codes for LGMD
ICD-10-CM codes for LGMD and several of its subtypes will be fully implemented and ready for use starting this October, MDA reports.
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Cancer Drug Shows Potential as Treatment for Muscular Dystrophy
An existing cancer drug could have potential as a treatment for muscular dystrophy, researchers suggest in a new study.
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Parent Project Muscular Dystrophy Hosts 28th Annual International Conference in Scottsdale, Ariz
Parent Project Muscular Dystrophy will host its 2022 Annual Conference in Scottsdale, Arizona, June 23-26.
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Avidity Biosciences Supports World FSHD Day and Presents Preclinical Data from Program
Avidity Biosciences Inc joins in activities to raise awareness for FSHD and highlights preclinical treatment results supporting AOC 1020.
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FSHD Society Convenes in Florida in June
The FSHD Society is holding back-to-back meetings in June in Orlando to help develop treatments for facioscapulohumeral muscular dystrophy.
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