Regenxbio to Trial Duchenne Muscular Dystrophy Gene Therapy
Regenxbio is recruiting for its Phase I/II Affinity Duchenne trial of the RGX-202 gene therapy treatment for Duchenne Muscular Dystrophy.
Category: Muscular Dystrophy
Muscular Dystrophy
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Muscular Dystrophy
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Most People with Spinal Muscular Atrophy Are Using New Gene Therapies, Per Survey
Health Union releases a survey that illuminates the perspectives and experiences of people living with spinal muscular atrophy.
Muscular Dystrophy
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RESTEM and JAR of Hope Foundation Announce Strategic Partnership and Clinical Trial Launch of Cell Therapy for Patients with Duchenne Muscular Dystrophy
RESTEM and JAR of Hope announce a strategic collaboration and launch of a clinical trial to evaluate RESTEM ULS therapy for Duchenne.
Bionic Clothing Maker CIONIC Collaborates with Yves Behar’s fuseproject
CIONIC announces a collaboration with acclaimed designer Yves Behar and his world-renowned multidisciplinary design firm, fuseproject.
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Parent Project Muscular Dystrophy Certifies Pittsburgh Clinic
Parent Project Muscular Dystrophy adds the clinic at UPMC Children’s Hospital of Pittsburgh to its Certified Duchenne Care Center Program.
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Fulcrum Phase 3 REACH FSHD Clinical Trial Using AMRA Medical’s MRI Measurements
Fulcrum Therapeutics is using AMRA Medical’s muscle fat infiltration (MFI) as a secondary endpoint in its phase 3 FSHD clinical trial: REACH.
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Parent Project Muscular Dystrophy (PPMD) Announces Pediatric Certified Duchenne Care Center at St Louis Children’s Hospital
Parent Project Muscular Dystrophy expands its Certified Duchenne Care Program with the certification of the first clinic in St. Louis.
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How Does Duchenne Muscular Dystrophy Cause Heart Rhythm Problems?
Mutations that cause Duchenne muscular dystrophy slow electrical activity in the heart, causing abnormal heart rhythms, a study notes.
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AMRA Medical Continues to Advance FSHD Research with Whole-Body Measurements
AMRA Medical publishes results of its Fulcrum-sponsored study highlighting the development and use of a MRI protocol for muscle analysis.
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Parent Project Muscular Dystrophy Nominates Duchenne for RUSP
Parent Project Muscular Dystrophy nominates Duchenne to be part of Recommended Uniform Screening Panel (RUSP) for newborns.
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LGMD Community Celebrates Adoption of ICD-10 Diagnostic Codes for LGMD
ICD-10-CM codes for LGMD and several of its subtypes will be fully implemented and ready for use starting this October, MDA reports.
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Cancer Drug Shows Potential as Treatment for Muscular Dystrophy
An existing cancer drug could have potential as a treatment for muscular dystrophy, researchers suggest in a new study.
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Parent Project Muscular Dystrophy Hosts 28th Annual International Conference in Scottsdale, Ariz
Parent Project Muscular Dystrophy will host its 2022 Annual Conference in Scottsdale, Arizona, June 23-26.
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Avidity Biosciences Supports World FSHD Day and Presents Preclinical Data from Program
Avidity Biosciences Inc joins in activities to raise awareness for FSHD and highlights preclinical treatment results supporting AOC 1020.
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FSHD Society Convenes in Florida in June
The FSHD Society is holding back-to-back meetings in June in Orlando to help develop treatments for facioscapulohumeral muscular dystrophy.
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Gamers: MDA Rivals Streaming Event Takes Place June 18
MDA Rivals on Saturday, June 18, aims to support funding for people living with muscular dystrophy, ALS, and related neuromuscular diseases.
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Muscular Dystrophy Association Celebrates Lou Gehrig Day at Major League Baseball Games in June
The Muscular Dystrophy Association will honor Major League Baseball’s recognition of Lou Gehrig Day at games across the country in June.
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SOLVE FSHD Supports the FSHD Canada Foundation in Funding of US$1.2M in Multidisciplinary Biomarker Grants
SOLVE FSHD announces its financial support to FSHD Canada Foundation’s grant funding to facilitate FSHD biomarker research.
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